Farzin Farzaneh
King’s College London, UK
Title: The translation of fundamental research discoveries into cell and gene based medicinal products
Biography
Biography: Farzin Farzaneh
Abstract
The therapeutic potential of cell and gene therapies has created a great deal of excitement in a range of biomedical fields. The path from fundamental research, through to licensing applications involves several important components. These include, studies assessing the validity of critical concepts, pre-clinical potential safety and efficacy studies, the design of clinical trials, production of products that are suitable for clinical investigations. Similarly important is the process leading to regulatory authorisation of clinical studies, the efficient conduct of meaningful clinical investigations, proof of concept and pivotal trials through to licensing applications. These processes constitute a complex path, with multiple critical steps and potential bottlenecks, involving important design and implementation challenges.
In an open discussion forum, some of the most prominent of these challenges will be identified and strategies to address them will be examined.